Muscular Dystrophy News23h
I’ll continue to do what I love, despite the FSHD ‘hangovers’
FSHD exacts a toll on columnist Robin Stemple when he is out and about. He calls these symptom flares "FSHD hangovers." ...
Muscular Dystrophy News2d
$10M in prizes offered toward work on FSHD treatments
Eight $250,000 prizes will be awarded for key milestones in FSHD treatments and $8 million will be given for showing clinical ...
Muscular Dystrophy News7d
Arrakis’ RNA-targeted oral therapies showing promise for DM1
Arrakis' oral therapies targeting disease-driving RNA in myotonic dystrophy have shown promise in preclinical studies.
Muscular Dystrophy News7d
When art and advocacy meet onstage
Columnist Shalom Lim describes a moving performance at the Enabling Lives Festival in Singapore, an example of the power of ...
Muscular Dystrophy News8d
Sarepta to develop Arrowhead’s muscular dystrophy treatments
Sarepta has acquired the global rights to develop ARO-DUX4 and ARO-DM1, two RNAi therapeutic candidates for types of muscular ...
Muscular Dystrophy News12d
Couch shopping awakened me to a focus on my children with DMD
Couch shopping made columnist Betty Vertin discover she was focused on her three children with DMD rather than the rest of her family.
Muscular Dystrophy News13d
DMD carrier with heart failure has healthy pregnancy: Case study
The case is reported of a young woman who began having DMD symptoms before getting pregnant, allowing her to receive genetic ...