Just six months after a newborn at Children's Hospital of Philadelphia was diagnosed with a rare and life-threatening metabolic disorder, doctors were able to develop a personalized treatment ...

A baby born with a rare and dangerous genetic disease is thriving after getting an experimental gene editing treatment made ...

KJ received the bespoke CRISPR treatment 6 1/2 months after birth, receiving three infusions of the therapy as of April 2025.

In a groundbreaking medical achievement, an infant from Pennsylvania, referred to as KJ, has become the first person to ...

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR gene editing therapy by a team at Children's Hospital of ...

In a world first, scientists used CRISPR to fix a baby's unique genetic mutation. The report offers hope for personalized ...

In addition to CFD simulation analysis, ABS took into account the latest industry best practices and advances in software and ...

A gene editing drug custom-made for a critically ill baby showed that, for some ultra-rare diseases, it’s possible to design ...

If an atmosphere is gaseous, it doesn't mean it's featureless and well mixed. In fact, Jupiter's atmosphere has structures scientists are still learning about.

KJ Muldoon was born with a devastating medical problem. Racing to solve it, doctors may have launched a 'roadmap' for a new ...

For the first time, doctors have created a customized treatment using the revolutionary gene-editing technique known as ...

A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.