Rare genetic diseases are challenging for patients and their families—made all the more overwhelming because symptoms tend to ...

UCD team uses novel polymer-based system to deliver corrective genes, an approach that appears to be better tolerated by ...

India offers a treasure trove of genetic data for AI-enabled researchers to develop therapies neglected by commercial ...

The gene-editing platform known as Crispr is widely used by researchers in scientific laboratories in their search for new ...

Fourteen million people worldwide suffer from enlarged hearts, or hypertrophic cardiomyopathy (HCM), a genetic disease that ...

Wave Life Sciences Ltd. shows promise with AATD, DMD, and Huntington's programs. Click for my updated look at WVE stock and ...

CRISPRware is a new tool scientists can use to design the best guide RNAs to edit genes in many organisms, without the need for deep bioinformatics expertise. By making gene editing more precise and ...

Prime Medicine, Inc. achieved strong early data in CGD with PM359, surpassing efficacy thresholds. Click here to find out why ...

Intellia Therapeutics NTLA has put up a stellar performance in the past month. Shares of the company have rallied 29.8% ...

Gabriella Ngang, of Farmington Hills, is one of three in Michigan to take part in a clinical trial of a new sickle cell ...

CRISPR is revolutionizing medicine by enabling precise DNA edits, treating genetic diseases like sickle cell anemia and ...