Rare genetic diseases are challenging for patients and their families—made all the more overwhelming because symptoms tend to ...

UCD team uses novel polymer-based system to deliver corrective genes, an approach that appears to be better tolerated by ...

India offers a treasure trove of genetic data for AI-enabled researchers to develop therapies neglected by commercial ...

The gene-editing platform known as Crispr is widely used by researchers in scientific laboratories in their search for new ...

Fourteen million people worldwide suffer from enlarged hearts, or hypertrophic cardiomyopathy (HCM), a genetic disease that ...

CRISPRware is a new tool scientists can use to design the best guide RNAs to edit genes in many organisms, without the need for deep bioinformatics expertise. By making gene editing more precise and ...

Prime Medicine, Inc. achieved strong early data in CGD with PM359, surpassing efficacy thresholds. Click here to find out why ...

Months after announcing an M&A deal with AstraZeneca, EsoBiotec has released the first small slice of data on the cell ...

New research has found a novel target with therapeutic potential for metastatic eye melanoma—an aggressive eye cancer—with ...

Intellia Therapeutics NTLA has put up a stellar performance in the past month. Shares of the company have rallied 29.8% ...