KJ received the bespoke CRISPR treatment 6 1/2 months after birth, receiving three infusions of the therapy as of April 2025.

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR gene editing therapy by a team at Children's Hospital of ...

In a world first, scientists used CRISPR to fix a baby's unique genetic mutation. The report offers hope for personalized ...

In addition to CFD simulation analysis, ABS took into account the latest industry best practices and advances in software and ...

The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific gene mutation, doctors say.

A gene editing drug custom-made for a critically ill baby showed that, for some ultra-rare diseases, it’s possible to design ...

If an atmosphere is gaseous, it doesn't mean it's featureless and well mixed. In fact, Jupiter's atmosphere has structures scientists are still learning about.

KJ Muldoon was born with a devastating medical problem. Racing to solve it, doctors may have launched a 'roadmap' for a new type of treatment.

For the first time, doctors have created a customized treatment using the revolutionary gene-editing technique known as ...

An infant named KJ has made history as the first patient to be treated with an in vivo CRISPR gene editing therapy designed ...

A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.

An infant in Philadelphia has been successfully treated with a customized Crispr gene-editing therapy for a rare and deadly ...