Melbourne scientists have shown for the first time how a “revolutionary” blood cancer treatment could be tweaked to also cure ...

CRISPR is revolutionizing medicine by enabling precise DNA edits, treating genetic diseases like sickle cell anemia and ...

“By uncovering specific genetic vulnerabilities like the CDS1 and CDS2 relationship, we’re opening the door to new therapies ...

Scientists at Fox Chase Cancer Center have identified a mutation in a common oncogene—a gene that can cause cancer—that may ...

Using gene editing in a preclinical model, researchers at UT Southwestern Medical Center blocked the symptoms of a rare smooth muscle disease before they developed. Their findings, published in ...

Cambridge-driven research has identified a novel target with therapeutic potential for metastatic eye melanoma — an ...

In a step toward treating mitochondrial diseases, researchers in the Netherlands have successfully edited harmful mutations ...

A gene-editing delivery system developed by UT Southwestern Medical Center researchers simultaneously targeted the liver and lungs of a preclinical model of a rare genetic disease known as alpha-1 ...

Cancer research no longer moves slowly; it advances rapidly. Revolutionary discoveries in precision medicine, immunotherapy, ...

Researchers have identified a mutation in a common oncogene that may play an important role in colon cancer. Their findings ...

Another gene-editing tool, CRISPR/Cas9 has been seen as the most sophisticated technology, but Sangamo has advanced faster into clinical trials than the numerous CRISPR innovators.