My baby daughter started pulling her hair out – now she’ll never walk, talk or live beyond 19
LUCY Glenn appeared “completely healthy” until she was 18 months old when her behaviour suddenly changed. Her mum, Katherine McCready, 31, said noticed she suddenly stopped playing ...
Medscape11d
Understanding, Recognizing, and Treating Rett Syndrome
The clinical picture of Rett syndrome is unique in that no other condition comprises a period of rapid mental and physical deterioration, followed by apparent stabilization or even improvement.
Study shows that Rett syndrome in females is not just less severe, but different
In the female mouse model with Rett syndrome, this gene impairment went in stages. The researchers called this "the seesaw ...
Marvel to File for Orphan Drug Designation with The U.S. FDA for MB-204 as a Treatment for Rett Syndrome
Marvel Biosciences Corp. (TSXV: MRVL) (OTCQB: MBCOF), and its wholly owned subsidiary, Marvel Biotechnology Inc.
Marvel Announces First of Two Final Data Sets from Rett Syndrome Study: MB-204 Significantly Outperforms Trofinetide
Marvel Biosciences Corp. (TSXV: MRVL) (OTCQB: MBCOF) and its wholly owned subsidiary, Marvel Biotechnology Inc. (collectively ...
Scioto Valley Guardian7d
Cincinnati researchers receive $2 million in grants for groundbreaking Rett Syndrome research
The International Rett Syndrome Foundation (IRSF), headquartered in Cincinnati, has announced the allocation of nearly $2 million in grants to seven leading researchers, ...
Morningstar19d
Clinical Data from Open-Label DAFFODIL™ Study Evaluating Long-term Safety of DAYBUE® (trofinetide) in Patients with Rett Syndrome Published in Med
Clinical Data from Open-Label DAFFODIL™ Study Evaluating Long-term Safety of DAYBUE® (trofinetide) in Patients with Rett Syndrome Published in Med -- Study supported FDA and Health Canada ...
Irish Sun4d
My baby daughter started pulling her hair out – now she’ll never walk, talk or live beyond 19
Rett syndrome is described in four stages, although symptoms will often overlap between each stage. During stage 3, some of the stage 2 symptoms may get better – for example, there may be ...