UCD team uses novel polymer-based system to deliver corrective genes, an approach that appears to be better tolerated by ...

Rare genetic diseases are challenging for patients and their families—made all the more overwhelming because symptoms tend to ...

Gabriella Ngang, of Farmington Hills, is one of three in Michigan to take part in a clinical trial of a new sickle cell ...

A man who was the first person in the UK to receive a groundbreaking gene-editing therapy on the NHS, said he felt " ...

Personalized CRISPR cures for children born with rare genetic diseases are now a step closer to being more widely available.

Last month, a baby got the world’s first personalized gene-editing treatment. What will this mean for millions of others with genetic diseases?

A new gene therapy trial safely restores hearing in deaf children and adults, offering hope for those with DFNB9 deafness ...

Emerging oligonucleotides and gene editing therapies offer greater precision, long-term efficacy, and improved adherence in comparison to traditional statin therapies. This is especially true for ...

We spoke with the developers and manufacturers of the CRISPR gene therapy used to treat KJ Muldoon’s rare genetic condition, ...

CRSP edges ahead of NTLA with the only approved CRISPR therapy, stronger pipeline breadth and recent stock gains.

Sangamo Therapeutics Inc. (NASDAQ:SGMO) ranks among the best CRISPR stocks to buy. Following the release of Sangamo ...

Melbourne scientists have shown for the first time how a “revolutionary” blood cancer treatment could be tweaked to also cure ...